Raffaella Origa
Differential effects of iron chelators on iron burden and long-term morbidity and mortality outcomes in a large cohort of transfusion-dependent β-thalassemia patients who remained on the same monotherapy over 10 years
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Deferasirox film-coated tablet-associated ulcerative colitis: An emerging pattern in thalassemia patients?
2024-01-01 Piolatto, A; Gaglioti, Cm; Tesio, N; Clemente, Mg; Culcasi, M; Matrone, A; Pila, Mp; Sambataro, A; Longo, F; Origa, R; Ferrero, Gb.
Unplanned pregnancy in women with beta-thalassaemia treated with luspatercept
2024-01-01 Zaccheddu, E; Zappu, A; Barella, S; Clemente, Mg; Orecchia, V; Pilia, Mp; Piras, S; Pitturru, C; Scarano, M; Origa, R.
Revisiting iron overload status and change thresholds as predictors of mortality in transfusion-dependent β-thalassemia: a 10-year cohort study
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Phenoconversion’ in adult patients with β-thalassemia
2024-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl
Atrial Fibrillation Prevalence and Its Management in Transfusion-Dependent Thalassemias: The Fathal Study
2023-01-01 Di Stefano, Valeria; Gianesin, Barbara; Bertini, Matteo; Culcasi, Martina; Rita Denotti, Anna; Derchi, Giorgio; Giuditta, Marianna; Longo, Filomena; Regina Manca, Maria; Cristina Martinoli, Maria; Orecchia, Valeria; Origa, Raffaella; Motta, Irene
Luspatercept in the Treatment of Beta Thalassemia in Italy: Lights and Shadows in Clinical Practice
2023-01-01 Gianesin, Barbara; Rosso, Rosamaria; Lisi, Roberto; Zappu, Antonietta; Motta, Irene; Longo, Filomena; Pinto, Valeria; Maria Grazia Sanna, Paola; De Franceschi, Lucia; Battista Ruffo, Giovan; DI Maggio, Rosario; Bulla, Anna; Ann Di Giorgio, Mary; Rita Denotti, Anna; Lello Panzieri, Daniele; Culcasi, Martina; Quintino, Sabrina; Marchisio, Andrea; Mazzi, Filippo; Miciotto, Francesca; Barone, Rita; Di Raimondo, Francesco; Ferraresi, Marta; Marchetti, Beatrice; Origa, Raffaella
Nephrological Complications in Hemoglobinopathies: SITE Good Practice
2023-01-01 Ruffo, Gb; Russo, R; Casini, T; Lombardini, L; Orecchia, V; Voi, V; Origa, R; Forni, Gl; Marchetti, M; Gigante, A; Garibotto, G; Maggio, A; De Franceschi, L.
Treating Thalassemia Patients with Luspatercept: An Expert Opinion Based on Current Evidence
2023-01-01 Longo, F; Motta, I; Pinto, V; Piolatto, A; Ricchi, P; Tartaglione, I; Origa, R.
Management of the Sickle Cell Trait: An Opinion by Expert Panel Members.
2023-01-01 Pinto, Vm; De Franceschi, L; Gianesin, B; Gigante, A; Graziadei, G; Lombardini, L; Palazzi, G; Quota, A; Russo, R; Sainati, L; Venturelli, D; Forni, Gl; Origa, R.
Reply to "Hepatocellular carcinoma in thalassemia and other hemoglobinopathies"
2023-01-01 Origa, R; Gianesin, B; Longo, F; Di Maggio, R; Cassinerio, E; Gamberini, Mr; Pinto, Vm; Casale, M; La Nasa, G; Caocci, G; Piroddi, A; Piolatto, A; Di Mauro, A; Romano, C; Gigante, A; Barella, S; Maggio, A; Graziadei, G; Perrotta, S; Forni, Gl.
Incidence of cancer and related deaths in hemoglobinopathies: A follow-up of 4631 patients between 1970 and 2021
2023-01-01 Origa, Raffaella; Gianesin, Barbara; Longo, Filomena; Di Maggio, Rosario; Cassinerio, Elena; Rita Gamberini, Maria; Maria Pinto, Valeria; Quarta, Antonella; Casale, Maddalena; LA NASA, Giorgio; Caocci, Giovanni; Piroddi, Antonio; Piolatto, Andrea; Di Mauro, Alessandra; Romano, Claudia; Gigante, Antonia; Barella, Susanna; Maggio, Aurelio; Graziadei, Giovanna; Perrotta, Silverio; Luca Forni, Gian
Hepatitis C and Thalassemia: A Story with (Almost) a Happy Ending
2023-01-01 Origa, Raffaella
Pretransfusion hemoglobin level and mortality in adults with transfusiondependent β-thalassemia
2023-01-01 Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl.
Safety and Efficacy of the New Combination Iron Chelation Regimens in Patients with Transfusion-Dependent Thalassemia and Severe Iron Overload
2022-01-01 Origa, R.; Cinus, M.; Pilia, M. P.; Gianesin, B.; Zappu, A.; Orecchia, V.; Clemente, M. G.; Pitturru, C.; Denotti, A. R.; Corongiu, F.; Piras, S.; Barella, S.
Tricuspid-valve regurgitant jet velocity as a risk factor for death in β-Thalassemia
2022-01-01 Derchi, Giorgio; Musallam, Khaled M.; Maria Pinto, Valeria; Graziadei, Giovanna; Giuditta, Marianna; Barella, Susanna; Origa, Raffaella; Casu, Gavino; Pasanisi, Annamaria; Longo, Filomena; Casale, Maddalena; Miceli, Roberta; Merella, Pierluigi; Gianesin, Barbara; Ameri, Pietro; Tartaglione, Immacolata; Perrotta, Silverio; Piga, Antonio; Domenica Cappellini, Maria; Gian Luca Forni, And
2021 Thalassaemia International Federation Guidelines for the Management of Transfusion-dependent Thalassemia
2022-01-01 Farmakis, D.; Porter, J.; Taher, A.; Cappellini, M. D.; Angastiniotis, M.; Eleftheriou, A.; Alassaf, A.; Angastiniotis, M.; Angelucci, E.; Aydinok, Y.; Bou-Fakhredin Rayan, R.; Brunetta, L.; Cappellini, M. D.; Constantinou, G.; Daar, S.; De Sanctis, V.; Dusheiko, G.; Elbard, R.; Eleftheriou, A.; Eleftheriou, P.; Englezos, P.; Farmakis, D.; Haines, D.; Hattab, F. N.; Kaltsounis, G.; Kattamis, A.; Koskinas, J.; Kumar, N.; Kulozik, A.; Kyriakou, A.; Maggio, A.; Maharai, R.; Mednick, L.; Michalaki, E.; Murphy, W.; Oevermann, L.; Origa, R.; Papayanni, P. -G.; Politis, C.; Porter, J.; Shah, F.; Skafi, A.; Skordis, N.; Sodani, P.; Soliman, A.; Subair, S.; Taher, A.; Tampaki, M.; Trompeter, S.; Tuli, S.; Walker, M.; Yamashita, R.; Yannaki, E.; Yardumian, A.
Crushed deferasirox film-coated tablets in pediatric patients with transfusional hemosiderosis: Results from a single-arm, interventional phase 4 study (MIMAS)
2022-01-01 Wali, Y.; Hassan, T.; Charoenkwan, P.; Trompeter, S.; Tartaglione, I.; Origa, R.; Gamberini, M. R.; Viprakasit, V.; Izquierdo, M.; Opio, S.; Roy, T.; Taher, A.
Mortality in β-thalassemia patients with confirmed pulmonary arterial hypertension on right heart catheterization
2022-01-01 Pinto, V. M.; Musallam, K. M.; Derchi, G.; Graziadei, G.; Giuditta, M.; Origa, R.; Barella, S.; Casu, G.; Pasanisi, A.; Longo, F.; Casale, M.; Miceli, R.; Merella, P.; Tartaglione, I.; Piga, A.; Cappellini, M. D.; Gianesin, B.; Forni, G. L.
Risk factors for endocrine complications in transfusion-dependent thalassemia patients on chelation therapy with deferasirox: a risk assessment study from a multicentre nation-wide cohort
2022-01-01 Casale, M; Forni, Gl; Cassinerio, E; Pasquali, D; Origa, R; Serra, M; Campisi, S; Peluso, A; Renni, R; Cattoni, A; De Michele, E; Allò, M; Poggi, M; Ferrara, F; Di Concilio, R; Sportelli, F; Quarta, A; Putti, Mc; Notarangelo, Ld; Sau, A; Ladogana, S; Tartaglione, I; Picariello, S; Marcon, A; Sturiale, P; Roberti, D; Lazzarino, Ai; Perrotta, S.
Transfusional Approach in Multi-Ethnic Sickle Cell Patients: Real-World Practice Data From a Multicenter Survey in Italy
2022-01-01 Graziadei, G; De Franceschi, L; Sainati, L; Venturelli, D; Masera, N; Bonomo, P; Vassanelli, A; Casale, M; Lodi, G; Voi, V; Rigano, P; Pinto, Vm; Quota, A; Notarangelo, Ld; Russo, G; Allo, M; Rosso, R; D'Ascola, D; Facchini, E; Macchi, S; Arcioni, F; Bonetti, F; Rossi, E; Sau, A; Campisi, S; Colarusso, G; Giona, F; Lisi, R; Giordano, P; Boscarol, G; Filosa, A; Marktel, S; Maroni, P; Murgia, M; Origa, R; Longo, F; Bortolotti, M; Colombatti, R; Di Maggio, R; Mariani, R; Piperno, A; Corti, P; Fidone, C; Palazzi, G; Badalamenti, L; Gianesin, B; Piel, Fb; Forni, Gl
The Management of Endocrine Complications in Patients with Haemoglobinopathies: Good Clinical Practice of the Italian Society of Thalassemia and Haemoglobinopathies (SITE)
2022-01-01 Casale, Maddalena; Baldini, Marina; Del Monte, Patrizia; Gigante, Antonia; Grandone, Anna; Origa, Raffaella; Poggi, Maurizio; Gadda, Franco; Lai, Rosalba; Marchetti, Monia; Luca Forni, Gian
Good Clinical Practice of the Italian Society of Thalassemia and Haemoglobinopathies (SITE) for the Management of Endocrine Complications in Patients with Haemoglobinopathies
2022-01-01 Casale, M; Baldini, Mi; Del Monte, P; Gigante, A; Grandone, A; Origa, R; Poggi, M; Gadda, F; Lai, R; Marchetti, M; Forni, Gl
Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
2021-01-01 Baronciani, D.; Casale, M.; De Franceschi, L.; Graziadei, G.; Longo, F.; Origa, R.; Rigano, P.; Pinto, V.; Marchetti, M.; Gigante, A.; Forni, G. L.
Hemoglobinopathies and Cancer: Preliminary Results of an Italian Multicenter Experience
2021-01-01 Origa, Raffaella; Longo, Filomena; Di Maggio, Rosario; Cassinerio, Elena; Maria Pinto, Valeria; Quarta, Antonella; Casale, Maddalena; Gianesin, Barbara; Barella, Susanna; Piolatto, Andrea; Maggio, Aurelio; Graziadei, Giovanna; Romano, Claudia; Perrotta, Silverio; Luca Forni, Gian
Changing patterns of thalassaemia in Italy: a WebThal perspective.
2021-01-01 Longo, F; Corrieri, P; Origa, R; Barella, S; Sanna, Pmg; Bitti, Pp; Zuccarelli, A; Commendatore, Fv; Vitucci, A; Quarta, A; Lisi, R; Cappellini, Md; Massei, F; Forni, Gl; Piga, A.
Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial
2020-01-01 Maggio, A; Kattamis, A; Felisi, M; Reggiardo, G; El-Beshlawy, A; Bejaoui, M; Sherief, L; Christou, S; Cosmi, C; Della Pasqua, O; Del Vecchio, Gc; Filosa, A; Cuccia, L; Hassab, H; Kreka, M; Origa, R; Putti, Mc; Spino, M; Telfer, P; Tempesta, B; Vitrano, A; Tsang, Yc; Zaka, A; Tricta, F; Bonifazi, D; Ceci, A.
A Phase 3 Trial of Luspatercept in Patients with Transfusion-Dependent β-Thalassemia
2020-01-01 Cappellini, Md; Viprakasit, V; Taher, At; Georgiev, P; Kuo, Khm; Coates, T; Voskaridou, E; Liew, Hk; Pazgal-Kobrowski, I; Forni, Gl; Perrotta, S; Khelif, A; Lal, A; Kattamis, A; Vlachaki, E; Origa, R; Aydinok, Y; Bejaoui, M; Ho, Pj; Chew, Lp; Bee, Pc; Lim, Sm; Lu, My; Tantiworawit, A; Ganeva, P; Gercheva, L; Shah, F; Neufeld, Ej; Thompson, A; Laadem, A; Shetty, Jk; Zou, J; Zhang, J; Miteva, D; Zinger, T; Linde, Pg; Sherman, Ml; Hermine, O; Porter, J; Piga, A; Believe, Investigators.
Two-year long safety and efficacy of deferasirox film-coated tablets in patients with thalassemia or lower/intermediate risk MDS: phase 3 results from a subset of patients previously treated with deferasirox in the ECLIPSE study
2020-01-01 Tartaglione, I; Origa, R; Kattamis, A; Pfeilstöcker, M; Gunes, S; Crowe, S; Fagan, N; Vincenzi, B; Ruffo, Gb.
Pregnancy in Thalassemia
2019-01-01 Origa, Raffaella; Comitini, Federica
Risk factors for heart disease in transfusion-dependent thalassemia: serum ferritin revisited
2019-01-01 Derchi, G; Dessì, C; Bina, P; Cappellini, Md; Piga, A; Perrotta, S; Tartaglione, I; Giuditta, M; Longo, F; Origa, R; Quarta, A; Pinto, V; Forni, Gl
Influence of patient-reported outcomes on the treatment effect of deferasirox film-coated and dispersible tablet formulations in the ECLIPSE trial: A post hoc mediation analysis
2019-01-01 Taher, At; Origa, R; Perrotta, S; Kouraklis, A; Belhoul, K; Huang, V; Han, J; Bruederle, A; Bobbili, P; Duh, Ms; Porter, Jb
Sotatercept, a novel transforming growth factor β ligand trap, improves anemia in β-thalassemia: a phase II, open-label, dose-finding study
2019-01-01 Cappellini, Md; Porter, J; Origa, R; Forni, Gl; Voskaridou, E; Galactéros, F; Taher, At; Arlet, Jb; Ribeil, Ja; Garbowski, M; Graziadei, G; Brouzes, C; Semeraro, M; Laadem, A; Miteva, D; Zou, J; Sung, V; Zinger, T; Attie, Km; Hermine, O.
Amustaline-glutathione pathogen-reduced red blood cell concentrates for transfusion-dependent thalassaemia
2019-01-01 Aydinok, Y; Piga, A; Origa, R; Mufti, N; Erickson, A; North, A; Waldhaus, K; Ernst, C; Lin, Js; Huang, N; Benjamin, Rj; Corash, L.
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia
2019-01-01 Marktel, S; Scaramuzza, S; Cicalese, Mp; Giglio, F; Galimberti, S; Lidonnici, Mr; Calbi, V; Assanelli, A; Bernardo, Me; Rossi, C; Calabria, A; Milani, R; Gattillo, S; Benedicenti, F; Spinozzi, G; Aprile, A; Bergami, A; Casiraghi, M; Consiglieri, G; Masera, N; D'Angelo, E; Mirra, N; Origa, R; Tartaglione, I; Perrotta, S; Winter, R; Coppola, M; Viarengo, G; Santoleri, L; Graziadei, G; Gabaldo, M; Valsecchi, Mg; Montini, E; Naldini, L; Cappellini, Md; Ciceri, F; Aiuti, A; Ferrari, G.
Selecting ß-Thalassemia Patients for Gene Therapy: A Decision-Making Algorithm
2019-01-01 Baronciani, D; Casale, M; De Franceschi, L; Graziadei, G; Longo, F; Origa, R; Pinto, Vm; Rigano, P; Marchetti, M; Gigante, A; Angelucci, E; Cappellini, Md; Iolascon, A; Piga, A; Forni, Gl.
Impact of the direct-acting antiviral agents (DAAs) on chronic hepatitis C in Sardinian patients with transfusion-dependent Thalassemia major
2019-01-01 Ponti, Ml; Comitini, F; Murgia, D; Ganga, R; Canu, R; Dessì, C; Foschini, Ml; Leoni, G; Morittu, M; Perra, M; Pilia, Mp; Casini, Mr; Zappu, A; Origa, R.
Quality of life in Sardinian patients with transfusion-dependent Thalassemia: a cross-sectional study
2018-01-01 Floris, F; Comitini, Federica; Leoni, G; Moi, P; Morittu, M; Orecchia, V; Perra, M; Pilia, Mp; Zappu, A; Casini, Mr; Origa, R.
Patient-reported outcomes from a randomized phase II study of the deferasirox film-coated tablet in patients with transfusion-dependent anemias
2018-01-01 Taher, At; Origa, R; Perrotta, S; Kouraklis, A; Ruffo, Gb; Kattamis, A; Goh, As; Huang, V; Zia, A; Herranz, Rm; Porter, Jb.
Hematological phenotypes in children according to the α-globin genotypes
2018-01-01 Origa, Raffaella; Barella, Susanna; Paglietti, Maria Elisabetta; Anni, Franco; Danjou, Fabrice; Denotti, Anna Rita; Desogus, Maria Franca; Loi, Daniela; Orecchia, Valeria; Sollaino, Maria Carla; Moi, Paolo
Renal safety under long-course deferasirox therapy in iron overloaded transfusion-dependent β-thalassemia and other anemias
2018-01-01 Origa, R; Piga, A; Tartaglione, I; Della Corte, G; Forni, Gl; Bruederle, A; Castiglioni, C; Han, J.
Transfusion Therapy in a Multi-Ethnic Sickle Cell Population Real-World Practice. a Preliminary Data Analysis of Multicentre Survey
2018-01-01 Graziadei, G; Sainati, L; Bonomo, P; Venturelli, D; Masera, N; Casale, M; Vassanelli, A; Lodi, Gl; Piel, Fb; Voi, V; De Franceschi, L; Rigano, P; Quota, A; Notarangelo, Ld; Russo, G; Rosso, R; Allò, M; D'Ascola, D; Facchini, E; Macchi, S; Arcioni, F; Piperno, A; Bonetti, F; Palazzi, G; Bisconte, Mg; Sau, A; Lisi, R; Giona, F; Campisi, S; Colarusso, G; Giordano, P; Boscariol, Gl; Marktel, S; Filosa, A; Origa, R; Murgia, M; Maroni, P; Gianesin, B; Badalamenti, L; Forni, Gl.
Hemoglobin Utilization in Asplenic and Non-Splenectomized Transfusion Dependent Thalassemia Patients Supported with Pathogen Reduced Red Blood Cell Concentrates in a Phase 3 Study (SPARC)
2018-01-01 Aydinok, Y; Piga, A; Origa, R; Mufti, N; Erikson, A; North, A; Waldhaus, K; Ernst, C; Lin, Js; Huang, N; ., Benjamin RJ; Corash, L.
The Believe Trial: Results of a Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Luspatercept in Adult Beta-Thalassemia Patients Who Require Regular Red Blood Cell (RBC) Transfusions
2018-01-01 Cappellini, Md; Viprakasit, V; Taher, A; Georgiev, P; Kuo, Khm; Coates, Td; Voskaridou, E; Liew, Hk; Pazgal-Kobrowski, I; Forni, Gl; Perrotta, S; Khelif, A; Lal, A; Kattamis, A; Vlachaki, E; Origa, R; Yesim, Aydinok; Bejaoui, M; Ho, Pj; Chew, Lp; Bee, Pc; Lim, Sm; Lu, My; Tantiworawit, A; Ganeva, P; Gercheva, L; Shah, F; Neufeld, Ej; Laadem, A; Shetty, Jk; Zou, J; Miteva, D; Zinger, T; Linde, Pg; Sherman, Ml; Hermine, O; Porter, J; Piga, A.
GDF15 and Erythroferrone Mark Erythropoietic Response to ACE-011 (Sotatercept) in Thalassemia
2018-01-01 Garbowski, Mw; Hermine, O; Cappellini, Md; Origa, R; Forni, Gl; Voskaridou, E; Galactéros, F; Taher, A; Arlet, Jb; Ribeil, Ja; Graziadei, G; Brouzes, C; Semeraro, M; Evans, P; Laadem, A; Miteva, D; Zou, J; Zinger, T; Schwickart, M; Sung, V; Porter, J.
Earlier initiation of transfusional and iron chelation therapies in recently born children with transfusion-dependent thalassemia
2017-01-01 Origa, Raffaella; Tatti, Federica; Zappu, Antonietta; Leoni, Giovan Battista; Dessì, Carlo; Moi, Paolo; Morittu, Maddalena; Orecchia, Valeria; Denotti, Anna Rita; Pilia, Maria Paola; Anni, Franco; Perra, Maria; Casini, Maria Rosaria; Barella, Susanna
New film-coated tablet formulation of deferasirox is well tolerated in patients with thalassemia or lower-risk MDS: Results of the randomized, phase II ECLIPSE study
2017-01-01 Taher, At; Origa, R; Perrotta, S; Kourakli, A; Ruffo, Gb; Kattamis, A; Goh, As; Cortoos, A; Huang, V; Weill, M; Merino Herranz, R; Porter, Jb
Treatment of hepatitis C virus infection with direct-acting antiviral drugs is safe and effective in patients with hemoglobinopathies
2017-01-01 Origa, R; Ponti, Ml; Filosa, A; Galeota Lanza, A; Piga, A; Saracco, Gm; Pinto, V; Picciotto, A; Rigano, P; Madonia, S; Rosso, R; D'Ascola, D; Cappellini, Md; D'Ambrosio, R; Tartaglione, I; De Franceschi, L; Gianesin, B; Di Marco, V; Forni, Gl
EPO and hepcidin plasma concentrations in blood donors and β-thalassemia intermedia are not related to commercially tested plasma ERFE concentrations
2017-01-01 Schotten, N; Laarakkers, Cm; Roelofs, Rw; Origa, R; van Kraaij, Mg; Swinkels, Dw
Causes of hospital admission in children and adults with transfusion-dependent thalassemia in Sardinia, 2000-2015
2017-01-01 Origa, Raffaella; Anni, Franco; Mereu, Luca; Follesa, Ilenia; Campus, Simona; Dessì, Carlo; Foschini, Maria Loreta; Leoni, Giovanbattista; Moi, Paolo; Morittu, Maddalena; Orecchia, Valeria; Perra, Maria; Zappu, Antonietta; Podda, Rosa Anna
Titolo | Data di pubblicazione | Autore(i) | Rivista | Editore |
---|---|---|---|---|
Differential effects of iron chelators on iron burden and long-term morbidity and mortality outcomes in a large cohort of transfusion-dependent β-thalassemia patients who remained on the same monotherapy over 10 years | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | BLOOD CELLS, MOLECULES, & DISEASES | - |
Deferasirox film-coated tablet-associated ulcerative colitis: An emerging pattern in thalassemia patients? | 1-gen-2024 | Piolatto, A; Gaglioti, Cm; Tesio, N; Clemente, Mg; Culcasi, M; Matrone, A; Pila, Mp; Sambataro, A; Longo, F; Origa, R; Ferrero, Gb. | BRITISH JOURNAL OF HAEMATOLOGY | - |
Unplanned pregnancy in women with beta-thalassaemia treated with luspatercept | 1-gen-2024 | Zaccheddu, E; Zappu, A; Barella, S; Clemente, Mg; Orecchia, V; Pilia, Mp; Piras, S; Pitturru, C; Scarano, M; Origa, R. | BRITISH JOURNAL OF HAEMATOLOGY | - |
Revisiting iron overload status and change thresholds as predictors of mortality in transfusion-dependent β-thalassemia: a 10-year cohort study | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | ANNALS OF HEMATOLOGY | - |
Phenoconversion’ in adult patients with β-thalassemia | 1-gen-2024 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl | AMERICAN JOURNAL OF HEMATOLOGY | - |
Atrial Fibrillation Prevalence and Its Management in Transfusion-Dependent Thalassemias: The Fathal Study | 1-gen-2023 | Di Stefano, Valeria; Gianesin, Barbara; Bertini, Matteo; Culcasi, Martina; Rita Denotti, Anna; Derchi, Giorgio; Giuditta, Marianna; Longo, Filomena; Regina Manca, Maria; Cristina Martinoli, Maria; Orecchia, Valeria; Origa, Raffaella; Motta, Irene | BLOOD | - |
Luspatercept in the Treatment of Beta Thalassemia in Italy: Lights and Shadows in Clinical Practice | 1-gen-2023 | Gianesin, Barbara; Rosso, Rosamaria; Lisi, Roberto; Zappu, Antonietta; Motta, Irene; Longo, Filomena; Pinto, Valeria; Maria Grazia Sanna, Paola; De Franceschi, Lucia; Battista Ruffo, Giovan; DI Maggio, Rosario; Bulla, Anna; Ann Di Giorgio, Mary; Rita Denotti, Anna; Lello Panzieri, Daniele; Culcasi, Martina; Quintino, Sabrina; Marchisio, Andrea; Mazzi, Filippo; Miciotto, Francesca; Barone, Rita; Di Raimondo, Francesco; Ferraresi, Marta; Marchetti, Beatrice; Origa, Raffaella | BLOOD | - |
Nephrological Complications in Hemoglobinopathies: SITE Good Practice | 1-gen-2023 | Ruffo, Gb; Russo, R; Casini, T; Lombardini, L; Orecchia, V; Voi, V; Origa, R; Forni, Gl; Marchetti, M; Gigante, A; Garibotto, G; Maggio, A; De Franceschi, L. | JOURNAL OF CLINICAL MEDICINE | - |
Treating Thalassemia Patients with Luspatercept: An Expert Opinion Based on Current Evidence | 1-gen-2023 | Longo, F; Motta, I; Pinto, V; Piolatto, A; Ricchi, P; Tartaglione, I; Origa, R. | JOURNAL OF CLINICAL MEDICINE | - |
Management of the Sickle Cell Trait: An Opinion by Expert Panel Members. | 1-gen-2023 | Pinto, Vm; De Franceschi, L; Gianesin, B; Gigante, A; Graziadei, G; Lombardini, L; Palazzi, G; Quota, A; Russo, R; Sainati, L; Venturelli, D; Forni, Gl; Origa, R. | JOURNAL OF CLINICAL MEDICINE | - |
Reply to "Hepatocellular carcinoma in thalassemia and other hemoglobinopathies" | 1-gen-2023 | Origa, R; Gianesin, B; Longo, F; Di Maggio, R; Cassinerio, E; Gamberini, Mr; Pinto, Vm; Casale, M; La Nasa, G; Caocci, G; Piroddi, A; Piolatto, A; Di Mauro, A; Romano, C; Gigante, A; Barella, S; Maggio, A; Graziadei, G; Perrotta, S; Forni, Gl. | CANCER | - |
Incidence of cancer and related deaths in hemoglobinopathies: A follow-up of 4631 patients between 1970 and 2021 | 1-gen-2023 | Origa, Raffaella; Gianesin, Barbara; Longo, Filomena; Di Maggio, Rosario; Cassinerio, Elena; Rita Gamberini, Maria; Maria Pinto, Valeria; Quarta, Antonella; Casale, Maddalena; LA NASA, Giorgio; Caocci, Giovanni; Piroddi, Antonio; Piolatto, Andrea; Di Mauro, Alessandra; Romano, Claudia; Gigante, Antonia; Barella, Susanna; Maggio, Aurelio; Graziadei, Giovanna; Perrotta, Silverio; Luca Forni, Gian | CANCER | - |
Hepatitis C and Thalassemia: A Story with (Almost) a Happy Ending | 1-gen-2023 | Origa, Raffaella | PATHOGENS | - |
Pretransfusion hemoglobin level and mortality in adults with transfusiondependent β-thalassemia | 1-gen-2023 | Musallam, Km; Barella, S; Origa, R; Ferrero, Gb; Lisi, R; Pasanisi, A; Longo, F; Gianesin, B; Forni, Gl. | BLOOD | - |
Safety and Efficacy of the New Combination Iron Chelation Regimens in Patients with Transfusion-Dependent Thalassemia and Severe Iron Overload | 1-gen-2022 | Origa, R.; Cinus, M.; Pilia, M. P.; Gianesin, B.; Zappu, A.; Orecchia, V.; Clemente, M. G.; Pitturru, C.; Denotti, A. R.; Corongiu, F.; Piras, S.; Barella, S. | JOURNAL OF CLINICAL MEDICINE | - |
Tricuspid-valve regurgitant jet velocity as a risk factor for death in β-Thalassemia | 1-gen-2022 | Derchi, Giorgio; Musallam, Khaled M.; Maria Pinto, Valeria; Graziadei, Giovanna; Giuditta, Marianna; Barella, Susanna; Origa, Raffaella; Casu, Gavino; Pasanisi, Annamaria; Longo, Filomena; Casale, Maddalena; Miceli, Roberta; Merella, Pierluigi; Gianesin, Barbara; Ameri, Pietro; Tartaglione, Immacolata; Perrotta, Silverio; Piga, Antonio; Domenica Cappellini, Maria; Gian Luca Forni, And | HAEMATOLOGICA | - |
2021 Thalassaemia International Federation Guidelines for the Management of Transfusion-dependent Thalassemia | 1-gen-2022 | Farmakis, D.; Porter, J.; Taher, A.; Cappellini, M. D.; Angastiniotis, M.; Eleftheriou, A.; Alassaf, A.; Angastiniotis, M.; Angelucci, E.; Aydinok, Y.; Bou-Fakhredin Rayan, R.; Brunetta, L.; Cappellini, M. D.; Constantinou, G.; Daar, S.; De Sanctis, V.; Dusheiko, G.; Elbard, R.; Eleftheriou, A.; Eleftheriou, P.; Englezos, P.; Farmakis, D.; Haines, D.; Hattab, F. N.; Kaltsounis, G.; Kattamis, A.; Koskinas, J.; Kumar, N.; Kulozik, A.; Kyriakou, A.; Maggio, A.; Maharai, R.; Mednick, L.; Michalaki, E.; Murphy, W.; Oevermann, L.; Origa, R.; Papayanni, P. -G.; Politis, C.; Porter, J.; Shah, F.; Skafi, A.; Skordis, N.; Sodani, P.; Soliman, A.; Subair, S.; Taher, A.; Tampaki, M.; Trompeter, S.; Tuli, S.; Walker, M.; Yamashita, R.; Yannaki, E.; Yardumian, A. | HEMASPHERE | - |
Crushed deferasirox film-coated tablets in pediatric patients with transfusional hemosiderosis: Results from a single-arm, interventional phase 4 study (MIMAS) | 1-gen-2022 | Wali, Y.; Hassan, T.; Charoenkwan, P.; Trompeter, S.; Tartaglione, I.; Origa, R.; Gamberini, M. R.; Viprakasit, V.; Izquierdo, M.; Opio, S.; Roy, T.; Taher, A. | AMERICAN JOURNAL OF HEMATOLOGY | - |
Mortality in β-thalassemia patients with confirmed pulmonary arterial hypertension on right heart catheterization | 1-gen-2022 | Pinto, V. M.; Musallam, K. M.; Derchi, G.; Graziadei, G.; Giuditta, M.; Origa, R.; Barella, S.; Casu, G.; Pasanisi, A.; Longo, F.; Casale, M.; Miceli, R.; Merella, P.; Tartaglione, I.; Piga, A.; Cappellini, M. D.; Gianesin, B.; Forni, G. L. | BLOOD | - |
Risk factors for endocrine complications in transfusion-dependent thalassemia patients on chelation therapy with deferasirox: a risk assessment study from a multicentre nation-wide cohort | 1-gen-2022 | Casale, M; Forni, Gl; Cassinerio, E; Pasquali, D; Origa, R; Serra, M; Campisi, S; Peluso, A; Renni, R; Cattoni, A; De Michele, E; Allò, M; Poggi, M; Ferrara, F; Di Concilio, R; Sportelli, F; Quarta, A; Putti, Mc; Notarangelo, Ld; Sau, A; Ladogana, S; Tartaglione, I; Picariello, S; Marcon, A; Sturiale, P; Roberti, D; Lazzarino, Ai; Perrotta, S. | HAEMATOLOGICA | - |
Transfusional Approach in Multi-Ethnic Sickle Cell Patients: Real-World Practice Data From a Multicenter Survey in Italy | 1-gen-2022 | Graziadei, G; De Franceschi, L; Sainati, L; Venturelli, D; Masera, N; Bonomo, P; Vassanelli, A; Casale, M; Lodi, G; Voi, V; Rigano, P; Pinto, Vm; Quota, A; Notarangelo, Ld; Russo, G; Allo, M; Rosso, R; D'Ascola, D; Facchini, E; Macchi, S; Arcioni, F; Bonetti, F; Rossi, E; Sau, A; Campisi, S; Colarusso, G; Giona, F; Lisi, R; Giordano, P; Boscarol, G; Filosa, A; Marktel, S; Maroni, P; Murgia, M; Origa, R; Longo, F; Bortolotti, M; Colombatti, R; Di Maggio, R; Mariani, R; Piperno, A; Corti, P; Fidone, C; Palazzi, G; Badalamenti, L; Gianesin, B; Piel, Fb; Forni, Gl | FRONTIERS IN MEDICINE | - |
The Management of Endocrine Complications in Patients with Haemoglobinopathies: Good Clinical Practice of the Italian Society of Thalassemia and Haemoglobinopathies (SITE) | 1-gen-2022 | Casale, Maddalena; Baldini, Marina; Del Monte, Patrizia; Gigante, Antonia; Grandone, Anna; Origa, Raffaella; Poggi, Maurizio; Gadda, Franco; Lai, Rosalba; Marchetti, Monia; Luca Forni, Gian | RECENTI PROGRESSI IN MEDICINA | - |
Good Clinical Practice of the Italian Society of Thalassemia and Haemoglobinopathies (SITE) for the Management of Endocrine Complications in Patients with Haemoglobinopathies | 1-gen-2022 | Casale, M; Baldini, Mi; Del Monte, P; Gigante, A; Grandone, A; Origa, R; Poggi, M; Gadda, F; Lai, R; Marchetti, M; Forni, Gl | JOURNAL OF CLINICAL MEDICINE | - |
Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm | 1-gen-2021 | Baronciani, D.; Casale, M.; De Franceschi, L.; Graziadei, G.; Longo, F.; Origa, R.; Rigano, P.; Pinto, V.; Marchetti, M.; Gigante, A.; Forni, G. L. | HEMASPHERE | - |
Hemoglobinopathies and Cancer: Preliminary Results of an Italian Multicenter Experience | 1-gen-2021 | Origa, Raffaella; Longo, Filomena; Di Maggio, Rosario; Cassinerio, Elena; Maria Pinto, Valeria; Quarta, Antonella; Casale, Maddalena; Gianesin, Barbara; Barella, Susanna; Piolatto, Andrea; Maggio, Aurelio; Graziadei, Giovanna; Romano, Claudia; Perrotta, Silverio; Luca Forni, Gian | BLOOD | - |
Changing patterns of thalassaemia in Italy: a WebThal perspective. | 1-gen-2021 | Longo, F; Corrieri, P; Origa, R; Barella, S; Sanna, Pmg; Bitti, Pp; Zuccarelli, A; Commendatore, Fv; Vitucci, A; Quarta, A; Lisi, R; Cappellini, Md; Massei, F; Forni, Gl; Piga, A. | BLOOD TRANSFUSION | - |
Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial | 1-gen-2020 | Maggio, A; Kattamis, A; Felisi, M; Reggiardo, G; El-Beshlawy, A; Bejaoui, M; Sherief, L; Christou, S; Cosmi, C; Della Pasqua, O; Del Vecchio, Gc; Filosa, A; Cuccia, L; Hassab, H; Kreka, M; Origa, R; Putti, Mc; Spino, M; Telfer, P; Tempesta, B; Vitrano, A; Tsang, Yc; Zaka, A; Tricta, F; Bonifazi, D; Ceci, A. | THE LANCET. HAEMATOLOGY | - |
A Phase 3 Trial of Luspatercept in Patients with Transfusion-Dependent β-Thalassemia | 1-gen-2020 | Cappellini, Md; Viprakasit, V; Taher, At; Georgiev, P; Kuo, Khm; Coates, T; Voskaridou, E; Liew, Hk; Pazgal-Kobrowski, I; Forni, Gl; Perrotta, S; Khelif, A; Lal, A; Kattamis, A; Vlachaki, E; Origa, R; Aydinok, Y; Bejaoui, M; Ho, Pj; Chew, Lp; Bee, Pc; Lim, Sm; Lu, My; Tantiworawit, A; Ganeva, P; Gercheva, L; Shah, F; Neufeld, Ej; Thompson, A; Laadem, A; Shetty, Jk; Zou, J; Zhang, J; Miteva, D; Zinger, T; Linde, Pg; Sherman, Ml; Hermine, O; Porter, J; Piga, A; Believe, Investigators. | NEW ENGLAND JOURNAL OF MEDICINE | - |
Two-year long safety and efficacy of deferasirox film-coated tablets in patients with thalassemia or lower/intermediate risk MDS: phase 3 results from a subset of patients previously treated with deferasirox in the ECLIPSE study | 1-gen-2020 | Tartaglione, I; Origa, R; Kattamis, A; Pfeilstöcker, M; Gunes, S; Crowe, S; Fagan, N; Vincenzi, B; Ruffo, Gb. | EXPERIMENTAL HEMATOLOGY & ONCOLOGY | - |
Pregnancy in Thalassemia | 1-gen-2019 | Origa, Raffaella; Comitini, Federica | MEDITERRANEAN JOURNAL OF HEMATOLOGY AND INFECTIOUS DISEASES | - |
Risk factors for heart disease in transfusion-dependent thalassemia: serum ferritin revisited | 1-gen-2019 | Derchi, G; Dessì, C; Bina, P; Cappellini, Md; Piga, A; Perrotta, S; Tartaglione, I; Giuditta, M; Longo, F; Origa, R; Quarta, A; Pinto, V; Forni, Gl | INTERNAL AND EMERGENCY MEDICINE | - |
Influence of patient-reported outcomes on the treatment effect of deferasirox film-coated and dispersible tablet formulations in the ECLIPSE trial: A post hoc mediation analysis | 1-gen-2019 | Taher, At; Origa, R; Perrotta, S; Kouraklis, A; Belhoul, K; Huang, V; Han, J; Bruederle, A; Bobbili, P; Duh, Ms; Porter, Jb | AMERICAN JOURNAL OF HEMATOLOGY | - |
Sotatercept, a novel transforming growth factor β ligand trap, improves anemia in β-thalassemia: a phase II, open-label, dose-finding study | 1-gen-2019 | Cappellini, Md; Porter, J; Origa, R; Forni, Gl; Voskaridou, E; Galactéros, F; Taher, At; Arlet, Jb; Ribeil, Ja; Garbowski, M; Graziadei, G; Brouzes, C; Semeraro, M; Laadem, A; Miteva, D; Zou, J; Sung, V; Zinger, T; Attie, Km; Hermine, O. | HAEMATOLOGICA | - |
Amustaline-glutathione pathogen-reduced red blood cell concentrates for transfusion-dependent thalassaemia | 1-gen-2019 | Aydinok, Y; Piga, A; Origa, R; Mufti, N; Erickson, A; North, A; Waldhaus, K; Ernst, C; Lin, Js; Huang, N; Benjamin, Rj; Corash, L. | BRITISH JOURNAL OF HAEMATOLOGY | - |
Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia | 1-gen-2019 | Marktel, S; Scaramuzza, S; Cicalese, Mp; Giglio, F; Galimberti, S; Lidonnici, Mr; Calbi, V; Assanelli, A; Bernardo, Me; Rossi, C; Calabria, A; Milani, R; Gattillo, S; Benedicenti, F; Spinozzi, G; Aprile, A; Bergami, A; Casiraghi, M; Consiglieri, G; Masera, N; D'Angelo, E; Mirra, N; Origa, R; Tartaglione, I; Perrotta, S; Winter, R; Coppola, M; Viarengo, G; Santoleri, L; Graziadei, G; Gabaldo, M; Valsecchi, Mg; Montini, E; Naldini, L; Cappellini, Md; Ciceri, F; Aiuti, A; Ferrari, G. | NATURE MEDICINE | - |
Selecting ß-Thalassemia Patients for Gene Therapy: A Decision-Making Algorithm | 1-gen-2019 | Baronciani, D; Casale, M; De Franceschi, L; Graziadei, G; Longo, F; Origa, R; Pinto, Vm; Rigano, P; Marchetti, M; Gigante, A; Angelucci, E; Cappellini, Md; Iolascon, A; Piga, A; Forni, Gl. | BLOOD | - |
Impact of the direct-acting antiviral agents (DAAs) on chronic hepatitis C in Sardinian patients with transfusion-dependent Thalassemia major | 1-gen-2019 | Ponti, Ml; Comitini, F; Murgia, D; Ganga, R; Canu, R; Dessì, C; Foschini, Ml; Leoni, G; Morittu, M; Perra, M; Pilia, Mp; Casini, Mr; Zappu, A; Origa, R. | DIGESTIVE AND LIVER DISEASE | - |
Quality of life in Sardinian patients with transfusion-dependent Thalassemia: a cross-sectional study | 1-gen-2018 | Floris, F; Comitini, Federica; Leoni, G; Moi, P; Morittu, M; Orecchia, V; Perra, M; Pilia, Mp; Zappu, A; Casini, Mr; Origa, R. | QUALITY OF LIFE RESEARCH | - |
Patient-reported outcomes from a randomized phase II study of the deferasirox film-coated tablet in patients with transfusion-dependent anemias | 1-gen-2018 | Taher, At; Origa, R; Perrotta, S; Kouraklis, A; Ruffo, Gb; Kattamis, A; Goh, As; Huang, V; Zia, A; Herranz, Rm; Porter, Jb. | HEALTH AND QUALITY OF LIFE OUTCOMES | - |
Hematological phenotypes in children according to the α-globin genotypes | 1-gen-2018 | Origa, Raffaella; Barella, Susanna; Paglietti, Maria Elisabetta; Anni, Franco; Danjou, Fabrice; Denotti, Anna Rita; Desogus, Maria Franca; Loi, Daniela; Orecchia, Valeria; Sollaino, Maria Carla; Moi, Paolo | BLOOD CELLS, MOLECULES, & DISEASES | - |
Renal safety under long-course deferasirox therapy in iron overloaded transfusion-dependent β-thalassemia and other anemias | 1-gen-2018 | Origa, R; Piga, A; Tartaglione, I; Della Corte, G; Forni, Gl; Bruederle, A; Castiglioni, C; Han, J. | AMERICAN JOURNAL OF HEMATOLOGY | - |
Transfusion Therapy in a Multi-Ethnic Sickle Cell Population Real-World Practice. a Preliminary Data Analysis of Multicentre Survey | 1-gen-2018 | Graziadei, G; Sainati, L; Bonomo, P; Venturelli, D; Masera, N; Casale, M; Vassanelli, A; Lodi, Gl; Piel, Fb; Voi, V; De Franceschi, L; Rigano, P; Quota, A; Notarangelo, Ld; Russo, G; Rosso, R; Allò, M; D'Ascola, D; Facchini, E; Macchi, S; Arcioni, F; Piperno, A; Bonetti, F; Palazzi, G; Bisconte, Mg; Sau, A; Lisi, R; Giona, F; Campisi, S; Colarusso, G; Giordano, P; Boscariol, Gl; Marktel, S; Filosa, A; Origa, R; Murgia, M; Maroni, P; Gianesin, B; Badalamenti, L; Forni, Gl. | BLOOD | - |
Hemoglobin Utilization in Asplenic and Non-Splenectomized Transfusion Dependent Thalassemia Patients Supported with Pathogen Reduced Red Blood Cell Concentrates in a Phase 3 Study (SPARC) | 1-gen-2018 | Aydinok, Y; Piga, A; Origa, R; Mufti, N; Erikson, A; North, A; Waldhaus, K; Ernst, C; Lin, Js; Huang, N; ., Benjamin RJ; Corash, L. | BLOOD | - |
The Believe Trial: Results of a Phase 3, Randomized, Double-Blind, Placebo-Controlled Study of Luspatercept in Adult Beta-Thalassemia Patients Who Require Regular Red Blood Cell (RBC) Transfusions | 1-gen-2018 | Cappellini, Md; Viprakasit, V; Taher, A; Georgiev, P; Kuo, Khm; Coates, Td; Voskaridou, E; Liew, Hk; Pazgal-Kobrowski, I; Forni, Gl; Perrotta, S; Khelif, A; Lal, A; Kattamis, A; Vlachaki, E; Origa, R; Yesim, Aydinok; Bejaoui, M; Ho, Pj; Chew, Lp; Bee, Pc; Lim, Sm; Lu, My; Tantiworawit, A; Ganeva, P; Gercheva, L; Shah, F; Neufeld, Ej; Laadem, A; Shetty, Jk; Zou, J; Miteva, D; Zinger, T; Linde, Pg; Sherman, Ml; Hermine, O; Porter, J; Piga, A. | BLOOD | - |
GDF15 and Erythroferrone Mark Erythropoietic Response to ACE-011 (Sotatercept) in Thalassemia | 1-gen-2018 | Garbowski, Mw; Hermine, O; Cappellini, Md; Origa, R; Forni, Gl; Voskaridou, E; Galactéros, F; Taher, A; Arlet, Jb; Ribeil, Ja; Graziadei, G; Brouzes, C; Semeraro, M; Evans, P; Laadem, A; Miteva, D; Zou, J; Zinger, T; Schwickart, M; Sung, V; Porter, J. | BLOOD | - |
Earlier initiation of transfusional and iron chelation therapies in recently born children with transfusion-dependent thalassemia | 1-gen-2017 | Origa, Raffaella; Tatti, Federica; Zappu, Antonietta; Leoni, Giovan Battista; Dessì, Carlo; Moi, Paolo; Morittu, Maddalena; Orecchia, Valeria; Denotti, Anna Rita; Pilia, Maria Paola; Anni, Franco; Perra, Maria; Casini, Maria Rosaria; Barella, Susanna | AMERICAN JOURNAL OF HEMATOLOGY | - |
New film-coated tablet formulation of deferasirox is well tolerated in patients with thalassemia or lower-risk MDS: Results of the randomized, phase II ECLIPSE study | 1-gen-2017 | Taher, At; Origa, R; Perrotta, S; Kourakli, A; Ruffo, Gb; Kattamis, A; Goh, As; Cortoos, A; Huang, V; Weill, M; Merino Herranz, R; Porter, Jb | AMERICAN JOURNAL OF HEMATOLOGY | - |
Treatment of hepatitis C virus infection with direct-acting antiviral drugs is safe and effective in patients with hemoglobinopathies | 1-gen-2017 | Origa, R; Ponti, Ml; Filosa, A; Galeota Lanza, A; Piga, A; Saracco, Gm; Pinto, V; Picciotto, A; Rigano, P; Madonia, S; Rosso, R; D'Ascola, D; Cappellini, Md; D'Ambrosio, R; Tartaglione, I; De Franceschi, L; Gianesin, B; Di Marco, V; Forni, Gl | AMERICAN JOURNAL OF HEMATOLOGY | - |
EPO and hepcidin plasma concentrations in blood donors and β-thalassemia intermedia are not related to commercially tested plasma ERFE concentrations | 1-gen-2017 | Schotten, N; Laarakkers, Cm; Roelofs, Rw; Origa, R; van Kraaij, Mg; Swinkels, Dw | AMERICAN JOURNAL OF HEMATOLOGY | - |
Causes of hospital admission in children and adults with transfusion-dependent thalassemia in Sardinia, 2000-2015 | 1-gen-2017 | Origa, Raffaella; Anni, Franco; Mereu, Luca; Follesa, Ilenia; Campus, Simona; Dessì, Carlo; Foschini, Maria Loreta; Leoni, Giovanbattista; Moi, Paolo; Morittu, Maddalena; Orecchia, Valeria; Perra, Maria; Zappu, Antonietta; Podda, Rosa Anna | ANNALS OF HEMATOLOGY | - |
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